Work

Pharmacology of a Central Nervous System Delivered 2′-O-Methoxyethyl–Modified Survival of Motor Neuron Splicing Oligonucleotide in Mice and Nonhuman Primates

Year: 2014

Type: article

Source: Journal of Pharmacology and Experimental Therapeutics

DOI: 10.1124/jpet.113.212407

Authors: Frank Rigo, Seung J. Chun, Daniel A. Norris, Gene Hung, Sam Lee, John Matson, Robert A. Fey, Hans Gaus, Yimin Hua, John S. Grundy, Adrian R. Krainer, Scott P. Henry, C. Frank Bennett

Institutions: Cold Spring Harbor Laboratory, Ionis Pharmaceuticals (United States)

Language: English

Topic: Neurogenetic and Muscular Disorders Research

Subfield: Genetics (clinical)

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: bronze

Funders: Spinal Muscular Atrophy Foundation, National Institute of General Medical Sciences

Awards: Biochemistry of Pre-mRNA Splicing, Biochemistry of Pre-mRNA Splicing

OpenAlex ID: W2090804804

FWCI: 17.98

Cites: 55

Cited by: 289

Related to: 10