Work

Enhancement of therapeutic transgene insertion for treatment of murine phenylketonuria

Year: 2025

Type: article

Abstract: .

Source: Molecular Therapy — Nucleic Acids

DOI: 10.1016/j.omtn.2025.102813

Authors: Michael A. Martinez, Daelyn Y. Richards, Shelley R. Winn, Adrian M. Baris, Anne Vonada, Laura Harper, Cary O. Harding

Institutions: Oregon Health & Science University, Washington State University Spokane

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: gold

Estimated APC paid: $3,900

Funder: National PKU Alliance

OpenAlex ID: W7117306381

FWCI: 2.207

Cites: 49

Cited by: 4

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