A First-in-human Phase I Study Demonstrating Safety, Tolerability, And Preliminary Efficacy Of RP-A601, An AAV-mediated Gene Therapy (AAVrh.74-PKP2a) In Adult Patients With PKP2-arrhythmogenic Cardiomyopathy (PKP2-ACM)
Year: 2026
Type: article
Study design: Clinical Trial
Source: Journal of Cardiac Failure
Institutions: University of California San Diego, Cranberry Institute
Language: English
Subfield: Cardiology and Cardiovascular Medicine
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W7123347916
