A Phase II Basket Trial of Vosoritide in Children with RASopathies, ACAN and NPR2 Deficiency - Supplementary Materials
Year: 2026
Type: article
Study design: Study Protocol
Abstract: These are supplementary data, a research protocol and statistical analysis plan that accompany a manuscript.
Source: Figshare
Author: Dauber, Andrew
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: green
OpenAlex ID: W7134935538
