Tofersen treatment in SOD1 p.Leu145Phe ALS: real-world outcomes in a genetically homogeneous Croatian cohort
Year: 2026
Type: article
Authors: Hrvoje Bilić, Marin Begović, Barbara Sitaš, Mirea Hančević, Branimir Ivan Šepec, Andrea Zemba Čilić, Vedrana Peček, Kristina Gotovac Jerčić, Josipa Mateševac, Tamara Bahčić, Laura Peček, Fran Borovečki, Niko Njirić, Jakob Nemir, Marina Petrović, Ivana Jurjević, Marijan Klarica, Iveta Merćep, Ervina Bilić
Institutions: University Hospital Centre Zagreb, University of Zagreb
Language: English
Subfield: Neurology
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W7135199496
