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Tofersen treatment in SOD1 p.Leu145Phe ALS: real-world outcomes in a genetically homogeneous Croatian cohort

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Year: 2026
Type: article
Source: Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration
DOI: 10.1080/21678421.2026.2638589
Authors: Hrvoje Bilić, Marin Begović, Barbara Sitaš, Mirea Hančević, Branimir Ivan Šepec, Andrea Zemba Čilić, Vedrana Peček, Kristina Gotovac Jerčić, Josipa Mateševac, Tamara Bahčić, Laura Peček, Fran Borovečki, Niko Njirić, Jakob Nemir, Marina Petrović, Ivana Jurjević, Marijan Klarica, Iveta Merćep, Ervina Bilić
Institutions: University Hospital Centre Zagreb, University of Zagreb
Language: English

Topic: Amyotrophic Lateral Sclerosis Research
Subfield: Neurology
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W7135199496
FWCI:
Cites: 16
Cited by:
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