A Multi-Center, Randomized, Double-Blind, Placebo-Controlled Trial to Evaluate the Neurological Effects of Encapsulated Dexamethasone Sodium Phosphate (eDSP) in Children with Ataxia Telangiectasia (NEAT)
Year: 2026
Type: preprint
Study designs: Randomized Controlled Trial, Clinical Trial
Source: SSRN Electronic Journal
DOI: 10.2139/ssrn.6399678
Authors: Sam Nicholas Russo, Stefan Zielen, Barbara Pietrucha, Jordis Trischler, Susan Perlman, Daniel Zielonka, Maria del Mar Garcia Romero, Winnie Ip, Asbjørg Stray-Pedersen, Malene Landbo Børresen, David Gomez-Andres, Samantha Lissauer, Jana Pachlopnik-Schmid, Konstantinos Karampatsas, Steve W. Wu, Francesco Pisani, Howard Lederman, Raffaele Badolato, Jan Kern, Oliver Kornmann, Helena Donath, William P. Whitehouse, Mary Kay Koenig, Hassan Abolhassani, Caralee Schaefer, Maureen Roden, Dirk Thye, Alex Smith, Biljana Horn, Andrew Prayle
Institutions: The University of Texas Health Science Center at Houston, Goethe University Frankfurt, Children's Memorial Health Institute, University of California, Los Angeles, Poznan University of Medical Sciences, Hospital Universitario La Paz, Great Ormond Street Hospital, Great Ormond Street Hospital for Children NHS Foundation Trust, Oslo University Hospital, University of Oslo, University of Copenhagen, Copenhagen University Hospital, Vall d'Hebron Hospital Universitari, University Hospitals Birmingham NHS Foundation Trust, University Children's Hospital Zurich, University of London, Cincinnati Children's Hospital Medical Center, Sapienza University of Rome, Johns Hopkins University, University of Brescia, University of Tübingen, University Hospital Frankfurt, University of Nottingham, University of Bonn, University Hospital Bonn, Nottingham University Hospitals NHS Trust
Language: English
Subfield: Cellular and Molecular Neuroscience
Field: Neuroscience
Domain: Life Sciences
Open Access status: green
OpenAlex ID: W7135204707
