Efficacité et sécurité à long terme d’omaveloxolone chez des patients atteints d’ataxie de Friedreich (AF) : données sur 4 ans issues de l’extension en ouvert MOXIe en cours
Year: 2026
Type: article
Source: Revue Neurologique
Authors: Theresa Zesiewicz, David R. Lynch, Martin B. Delatycki, J. Chad Hoyle, Sylvia Boesch, Wolfgang Nachbauer, Paola Giunti, George Wilmot, Sub H. Subramony, Katherine D. Mathews, Susan Perlman, Richard Lawson, Changyu Shen, Syed Syed Farooq, Shobhana Natarajan, Rose Domingo-Horne, Andre Arizpe, Nicolas Folschweiller, Masako Murai
Institutions: University of South Florida, Children's Hospital of Philadelphia, Victorian Clinical Genetics Services, Murdoch Children's Research Institute, The Ohio State University, Innsbruck Medical University, Universität Innsbruck, University College London, Emory University, University of Florida Health, University of Florida, University of Iowa, University of California, Los Angeles, Biogen (United States), Biogen (Switzerland)
Language: French
Subfield: Cellular and Molecular Neuroscience
Field: Neuroscience
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W7140194313
