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Efficacité et sécurité à long terme d’omaveloxolone chez des patients atteints d’ataxie de Friedreich (AF) : données sur 4 ans issues de l’extension en ouvert MOXIe en cours

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Year: 2026
Type: article
Source: Revue Neurologique
DOI: 10.1016/j.neurol.2026.01.185
Authors: Theresa Zesiewicz, David R. Lynch, Martin B. Delatycki, J. Chad Hoyle, Sylvia Boesch, Wolfgang Nachbauer, Paola Giunti, George Wilmot, Sub H. Subramony, Katherine D. Mathews, Susan Perlman, Richard Lawson, Changyu Shen, Syed Syed Farooq, Shobhana Natarajan, Rose Domingo-Horne, Andre Arizpe, Nicolas Folschweiller, Masako Murai
Institutions: University of South Florida, Children's Hospital of Philadelphia, Victorian Clinical Genetics Services, Murdoch Children's Research Institute, The Ohio State University, Innsbruck Medical University, Universität Innsbruck, University College London, Emory University, University of Florida Health, University of Florida, University of Iowa, University of California, Los Angeles, Biogen (United States), Biogen (Switzerland)
Language: French

Topic: Genetic Neurodegenerative Diseases
Subfield: Cellular and Molecular Neuroscience
Field: Neuroscience
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W7140194313
FWCI:
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Related to: 10
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