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Amino acid-derived ionizable lipids enable inhaled base editing for therapeutic gene correction in the lung

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Year: 2026
Type: article
Source: Nature Materials
DOI: 10.1038/s41563-026-02555-0
Authors: Fanglin Gong, Yue Xu, Jingan Chen, Shun Zhang, Songtao Dong, Lauren Healy, Breanna Seto, Muye Zhou, Rick Xing Ze Lu, Gen Li, Tyler Thomson, Yinghua Tang, Ziyan Chen, Krista Antonio, Andrew Varley, David X. W. Chen, Craig A. Hodges, Amy P. Wong, Jim Hu, Basil P. Hubbard, John F. Engelhardt, Ziying Yan, Bowen Li
Institutions: University of Toronto, University of Iowa, University of Alabama at Birmingham, Hospital for Sick Children, University of British Columbia, Case Western Reserve University, University Health Network, Princess Margaret Cancer Centre
Language: English

Topic: RNA Interference and Gene Delivery
Subfield: Molecular Biology
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W7147121507
FWCI: 14.58
Cites: 79
Cited by: 8
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