Work

Evolving landscape of drug development for pediatric rare diseases–from successes to strategies for addressing unmet needs

Year: 2026

Type: review

Source: Journal of Pharmaceutical Sciences

DOI: 10.1016/j.xphs.2026.104401

Authors: Sydney Stern, Yifei Zhang, Michelle Pressly, Xinning Yang, Susan Abdel-Rahman, Jie Wang, Mei-Chuan Chen, Chun-Han Chen, Salvatore Pepe, Mary Doi, Gilbert J. Burckart, Lynne P Yao, Robert Schuck, Jane PF Bai

Institutions: United States Food and Drug Administration, Center for Drug Evaluation and Research, Taipei Medical University

Language: English

Topic: Pharmaceutical studies and practices

Subfield: Pediatrics, Perinatology and Child Health

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: green

OpenAlex ID: W7165387259

FWCI:

Cites: 74

Cited by:

Related to: 10