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Precision metabolic therapy for propionic acidemia

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Year: 2026
Type: article
Source: Biochemical Pharmacology
DOI: 10.1016/j.bcp.2026.118187
Authors: Boopathi Subramaniyan, Fang Lu, Huan Li, Chorlada Paiboonrungruang, Yahui Li, Zhaohui Xiong, Guo-Fang Zhang, Xiaoxin Chen
Institutions: Cooper University Hospital, Cooper University Health Care, Duke University, Coriell Institute For Medical Research, Duke Medical Center
Language: English

Topic: Metabolism and Genetic Disorders
Subfield: Clinical Biochemistry
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: green

Funders: Propionic Acidemia Foundation, National Institutes of Health, National Center for Advancing Translational Sciences
Award: G1559423802
OpenAlex ID: W7165808766
FWCI:
Cites: 125
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