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Ora visual navigation course™ mobility test results in two individuals with CEP290 LCA after intravitreal injection of antisense oligonucleotide

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Year: 2026
Type: article
Source: Ophthalmic Genetics
DOI: 10.1080/13816810.2026.2692066
Authors: Caio Marques, Gabriela Doná Rodrigues, Ester Abigail da Silva Martins, Pedro Henrique Soares Nunes, Luci Meire Pereira da Silva, Cristina Muccioli, Adriana Berezovsky, Nívea Nunes Ferraz, Paula Yuri Sacai, Mariana Vallim Salles, Rebeca Azevedo Souza Amaral, Mariana Matioli da Palma, Érika Sayuri Yasaki, Huber Martins Vasconcelos Junior, Franc Toro, Christian Sundstrom, Marin Caka, Michael R. Schwartz, Zuhal Butuner, Juliana Maria Ferraz Sallum
Institution: Thea (France)
Language: English

Topic: Retinal Development and Disorders
Subfield: Molecular Biology
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed

Funders: Coordenação de Aperfeiçoamento de Pessoal de Nível Superior, ProQR Therapeutics
OpenAlex ID: W7165929038
FWCI:
Cites: 17
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