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SPL84 and Trikafta® exhibit comparable and additive effects in patient-derived HBE cells carrying the 3849+10kb C→T/F508del CFTR variants

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Year: 2026
Type: article
Source: Journal of Cystic Fibrosis
DOI: 10.1016/j.jcf.2026.06.005
Authors: Yi Cheng, Yifat S. Oren, Jan Harrington, Aurélie Hatton, Efrat Ozeri-Galai, Chava D. Stampfer, Tamar Mordechai, Ofra Barchad-Avitzur, Gili Hart, Kevin Coote, Hermann Bihler, Isabelle Sermet-Gaudelus, Martin Mense, Batsheva Kerem
Institutions: Cystic Fibrosis Foundation, Hadassah Medical Center, Inserm, Institut Necker Enfants Malades, Hebrew University of Jerusalem
Language: English

Topic: Cystic Fibrosis Research Advances
Subfield: Pulmonary and Respiratory Medicine
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W7166191358
FWCI:
Cites: 28
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