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L-citrulline treatment of nitric oxide deficiency in MELAS a phase I dose-finding and safety study

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Year: 2026
Type: article
Study design: Clinical Trial
Source: Molecular Genetics and Metabolism
DOI: 10.1016/j.ymgme.2026.110209
Authors: Mohammed Almannai, Jimmy Duong, Ayman W. El-Hattab, May Ali, Dianne Bauri, Nathan Hawk, Claudia Soler-Alfonso, Lacey Delay, Zili D. Chu, Ning Liu, Charul Gijavanekar, Sarah H. Elsea, Stephen F. Kralik, Shing Lee, Fernando Scaglia
Institutions: King Saud bin Abdulaziz University for Health Sciences, King Abdulaziz Medical City, King Abdullah International Medical Research Center, National Guard Health Affairs, Columbia University, Khalifa University of Science and Technology, Baylor College of Medicine, Cincinnati Children's Hospital Medical Center, Texas Children's Hospital, Baylor Genetics, Prince of Wales Hospital
Language: English

Topic: Neurological Disorders and Treatments
Subfield: Neurology
Field: Neuroscience
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: green

Funder: Foundation for the National Institutes of Health
OpenAlex ID: W7168257538
FWCI:
Cites: 55
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