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Leveraging host-cell modulators of adeno-associated vector transduction to tailor viral biodistribution

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Year: 2026
Type: article
Source: Molecular Therapy
DOI: 10.1016/j.ymthe.2026.08.024
Authors: Katie Kubek-Luck, Jason Velazquez, Xiaorui Yao, Joseph Gabriels, Charles Hsu, Sanjay Arora, Lara Bontadelli, Yoann Gilbart, Fumiaki Aihara, Hui Li, Fadela Bouadjemi, James Ooi, Jairo Nunes, Frederic Sigoillot, Jan Weiler, Emily Meseck, Keith Mansfield, Eloise Hudry
Institutions: Novartis (Switzerland), Novartis Institutes for BioMedical Research, Novartis (United States)
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: green
OpenAlex ID: W7203832111
FWCI:
Cites: 70
Cited by:
Related to: 10
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