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Hepatotoxicity in Adeno-Associated Virus Gene Therapy: Clinical Challenges and Strategic Solutions

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Year: 2026
Type: article
Source: The Journal of Pediatrics
DOI: 10.1016/j.jpeds.2026.115317
Authors: Akihiro Asai, Amal Aqul, Anna M. Banc-Husu, Tamir Diamond, Scott A. Elisofon, A. Jay. Freeman, Kathleen M. Loomes, Saeed Mohammad, Shikha S. Sundaram, Catherine A. Chapin
Institutions: Cincinnati Children's Hospital Medical Center, University of Cincinnati, The University of Texas Southwestern Medical Center, Baylor College of Medicine, Texas Children's Hospital, Children's Hospital of Philadelphia, University of Pennsylvania, Boston Children's Hospital, Harvard University, Nationwide Children's Hospital, The Ohio State University, Monroe Carell Jr. Children's Hospital, Vanderbilt University Medical Center, Children's Hospital Colorado, University of Colorado Anschutz, Northwestern University, Lurie Children's Hospital
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W7208823245
FWCI:
Cites: 23
Cited by:
Related to: 10
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