Is hematopoietic stem cell transplantation indicated in THPO-mutated congenital amegakaryocytic thrombocytopenia? Comment on: "Avatrombopag as a novel salvage therapy for refractory thrombocytopenia in THPO-mutated congenital amegakaryocytic thrombocytopenia after allogeneic hematopoietic stem cell transplantation"
Year: 2026
Type: article
Abstract: Not available.
Source: Haematologica
Authors: Paul Saultier, Alessandro Pecci
Institutions: Aix-Marseille Université, University of Pavia
Language: English
Subfield: Hematology
Field: Medicine
Domain: Health Sciences
Open Access status: gold
Estimated APC paid: $2,157
OpenAlex ID: W7222017401
FWCI:
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