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Brain gene therapy for metachromatic leukodystrophy: towards clinical trial

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Year: 2010
Type: article
Source: HAL
Authors: Piguet, F., Sondhi, D., Colle, Marie-Anne, Raoul, Solène, Roujeau, T., Piraud, M., Ahouansou, O., Bouquet, C., Vanier, M.T., Moullier, P., Cherel, Yan, Hackett, N.R, Zerah, M., Aubourg, P., Crystal, R.G., Cartier, N., Sevin, C.
Institutions: Inserm, Cornell University, Centre Hospitalier Universitaire de Nantes, Nantes Université, Hôpital Necker-Enfants Malades, Assistance Publique – Hôpitaux de Paris
Language: English

Topic: Lysosomal Storage Disorders Research
Subfield: Physiology (medical)
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W773131709
FWCI: 0.203
Cites:
Cited by: 1
Related to: 10
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