Author

Louise Himmelstrup

OpenAlex ID: A5117724924

Long-term efficacy and safety of arimoclomol in Niemann-Pick disease type C: Final results of the phase 2/3 NPC-002 48-month open-label extension trial

2025 · Eugen Mengel, Rosalia M. Da Riol, et al. · Molecular Genetics and Metabolism · 5

Efficacy results from a 12-month double-blind randomized trial of arimoclomol for treatment of Niemann-Pick disease type C (NPC): Presenting a rescored 4-domain NPC Clinical Severity Scale

2025 · Eugen Mengel, Marc C. Patterson, et al. · Molecular Genetics and Metabolism Reports · 1

Perseverance is key for regulatory success in ultra-rare diseases - Key learnings from arimoclomol's regulatory journey

2025 · Louise Himmelstrup, Anya Adamson · Molecular Genetics and Metabolism

Works count: 3

Citation count: 6

H-index: 1

I10-index: