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Chad Koehler
Institution:
BioMarin (United States)
Observed institution:
BioMarin (United States)
OpenAlex ID:
A5139727492
Sequence determinants of efficient exon 44 skipping in Duchenne muscular dystrophy define design principles for steric-blocking antisense oligonucleotides
2026
·
Enyang Han
, Katherine Webster
, et al.
·
bioRxiv (Cold Spring Harbor Laboratory)
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