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10748
Funder:
Rosetrees Trust
Funded outputs count:
4
Funder award ID:
10748
OpenAlex ID:
G799129384
mRNA-LNP therapy restores systemic nucleoside imbalance in a mitochondrial DNA depletion syndrome
2026
·
Nissa L Carrodus
, Jenny J Yang
, et al.
·
bioRxiv (Cold Spring Harbor Laboratory)
PDF
Consensus Recommendations for the Clinical Management of Wolfram syndrome Using a Delphi Method
2026
·
Josephine Elliott
, Saumel Ahmadi
, et al.
·
medRxiv
·
2
PDF
Recessive variants in mitochondrial complex I nuclear subunits are an underrated cause of optic atrophy
2025
·
Claudio Fiorini
, Neringa Jurkute
, et al.
·
Brain
·
3
PDF
CRISPRa-Mediated Increase of OPA1 Expression in Dominant Optic Atrophy
2025
·
Giada Becchi
, Michael Whitehead
, et al.
·
International Journal of Molecular Sciences
·
2
PDF
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