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A Phase 2a, Open-Label, Dose-Finding Study To Determine The Safety and Tolerability Of Sotatercept (ACE-011) In Adults With Beta (β)-Thalassemia: Interim Results

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Year: 2013
Type: article
Source: Blood
DOI: 10.1182/blood.v122.21.3448.3448
Authors: Maria-Domenica Cappellini, John Porter, Raffaella Origa, Gian Luca Forni, Adberrahmane Laadem, Frédéric Galacteros, Dimana Miteva, Victoria Sung, Rajesh Chopra, Jean-Benoît Arlet, Jean-Antoine Ribeil, Kenneth Klesczewski, Kenneth Attie, Maciej Garbowski, Olivier Hermine
Institutions: University of Milan, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, University College London, University of Cagliari, Ospedale Microcitemico, Ente Ospedaliero Ospedali Galliera, Celgene (United States), Centre Hospitalier Universitaire Henri-Mondor, Hôpitaux Universitaires Henri-Mondor, Hôpital Necker-Enfants Malades, Institut des Maladies Génétiques Imagine, Acceleron Pharma (United States)
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W1344043
FWCI: 1.147
Cites:
Cited by: 15
Related to: 10
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