Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response
Year: 2006
Type: article
Source: Nature Medicine
DOI: 10.1038/nm1358
Authors: Catherine S Manno, Glenn F Pierce, Valder R Arruda, Bertil Glader, Margaret Ragni, John J E Rasko, Margareth C Ozelo, Keith Hoots, Philip Blatt, Barbara Konkle, Michael Dake, Robin Kaye, Mahmood Razavi, Albert Zajko, James Zehnder, Pradip Rustagi, Hiroyuki Nakai, Amy Chew, Debra Leonard, J Fraser Wright, Ruth R Lessard, Jürg M Sommer, Michael Tigges, Denise Sabatino, Alvin Luk, Haiyan Jiang, Federico Mingozzi, Linda Couto, Hildegund C Ertl, Katherine A High, Mark A Kay
Institutions: Children's Hospital of Philadelphia, University of Pennsylvania, Stanford Medicine, Stanford University, Hemophilia Center of Western Pennsylvania, University of Pittsburgh Medical Center, Royal Prince Alfred Hospital, Centenary Institute, Universidade Estadual de Campinas (UNICAMP), The University of Texas Health Science Center at Houston, Christiana Hospital, Penn Presbyterian Medical Center, Cornell University, The Wistar Institute, Howard Hughes Medical Institute
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W1976329054