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O136 A NOVEL, HYBRID RECOMBINANT AAV-piggyBac TRANSPOSON VECTOR PERMITS ROBUST LONG-TERM PHENOTYPE CORRECTION OF THE PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS TYPE 3 MOUSE MODEL IN VIVO

Year: 2014
Type: conference-abstract
Language: English
Subfield: Genetics
Open Access status: closed
OpenAlex ID: W2005242532
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Cited by: 1
Related to: 10