A contradictory treatment for lysosomal storage disorders: inhibitors enhance mutant enzyme activity
Year: 2003
Type: review
Author: Jian-Qiang Fan
Institution: Icahn School of Medicine at Mount Sinai
Language: English
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
Open Access status: closed
Funder: Amicus Therapeutics
OpenAlex ID: W2011709758
