Work

Nonclinical evaluation of CNS-administered TPP1 enzyme replacement in canine CLN2 neuronal ceroid lipofuscinosis

Year: 2014

Type: article

Source: Molecular Genetics and Metabolism

DOI: 10.1016/j.ymgme.2014.09.004

Authors: Brian R. Vuillemenot, Derek Kennedy, Jonathan D. Cooper, Andrew M.S. Wong, Sarmi Sri, Thom Doeleman, Martin L. Katz, Joan R. Coates, Gayle C. Johnson, Randall P. Reed, Eric L. Adams, Mark T. Butt, Donald G. Musson, Joshua Henshaw, Steve Keve, Rhea Cahayag, Laurie S. Tsuruda, Charles A. O'Neill

Institutions: BioMarin (United States), King's College London, University of Missouri

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

Funder: BioMarin Pharmaceutical

OpenAlex ID: W2052298217

FWCI: 4.468

Cites: 39

Cited by: 60

Related to: 10