Long-term correction of hyperphenylalaninemia by AAV-mediated gene transfer leads to behavioral recovery in phenylketonuria mice
Year: 2004
Type: article
Source: Gene Therapy
Authors: S Mochizuki, H Mizukami, T Ogura, S Kure, A Ichinohe, K Kojima, Y Matsubara, E Kobayahi, T Okada, A Hoshika, K Ozawa, A Kume
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W2099863559
