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Gene editing of DNAH11 restores normal cilia motility in primary ciliary dyskinesia

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Year: 2016
Type: article
Source: Journal of Medical Genetics
DOI: 10.1136/jmedgenet-2015-103539
Authors: Michele Lai, Massimo Pifferi, Andrew Bush, Martina Piras, Angela Michelucci, Maria Di Cicco, Ambra del Grosso, Paola Quaranta, Chiara Cursi, Elena Tantillo, Sara Franceschi, Maria Chiara Mazzanti, Paolo Simi, Giuseppe Saggese, Attilio Boner, Mauro Pistello
Institutions: University of Pisa, Azienda Ospedaliera Universitaria Pisana, Royal Brompton Hospital, Fondazione Arpa, Fondazione Pisa, University of Verona
Language: English

Topic: Cystic Fibrosis Research Advances
Subfield: Pulmonary and Respiratory Medicine
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2265028954
FWCI: 5.579
Cites: 53
Cited by: 76
Related to: 10
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