Work

Enzyme therapy in Gaucher disease type 1: dosage efficacy and adverse effects in 33 patients treated for 6 to 24 months

Year: 1993

Type: article

Source: Blood

DOI: 10.1182/blood.v82.2.408.408

Authors: GM Pastores, AR Sibille, GA Grabowski

Institution: Icahn School of Medicine at Mount Sinai

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Genetics (clinical)

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

Funders: National Institute of Diabetes and Digestive and Kidney Diseases, National Center for Research Resources

Awards: Studies of Gaucher Disease: A Prototype Lipidosis, G3136012109

OpenAlex ID: W230215977

FWCI: 10.25

Cites: 17

Cited by: 174

Related to: 10