Work

Gene therapies that restore dystrophin expression for the treatment of Duchenne muscular dystrophy

Year: 2016

Type: article

Source: Human Genetics

DOI: 10.1007/s00439-016-1725-z

Authors: Jacqueline N. Robinson-Hamm, Charles A. Gersbach

Institutions: Duke University, Duke Medical Center

Language: English

Topic: Muscle Physiology and Disorders

Subfield: Molecular Biology

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: green

Funders: Muscular Dystrophy Association, National Institutes of Health, National Institute of Arthritis and Musculoskeletal and Skin Diseases, Medical Research and Materiel Command

Awards: Engineering Morphogenetic Factors for Enhanced Genetic Reprogramming, G4782616887, CRISPR/Cas9-Based Gene Editing for the Correction of Duchenne Muscular Dystrophy, G8595680174

OpenAlex ID: W2518024229

FWCI: 6.926

Cites: 135

Cited by: 69

Related to: 10