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Characterization of Dysphagia and Longitudinal Changes in Swallowing Function in Adults with Niemann-Pick Disease Type C Treated with Miglustat

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Year: 2020
Type: article
Source: Dysphagia
DOI: 10.1007/s00455-020-10145-8
Authors: Courtney Lewis, Megan Keage, Miyuki Watanabe, Danielle Schubiger, Dennis Velakoulis, Mark Walterfang, Adam P. Vogel
Institutions: The University of Melbourne, Monash Health, The Royal Melbourne Hospital, Florey Institute of Neuroscience and Mental Health, Hertie Institute for Clinical Brain Research, University of Tübingen
Language: English

Topic: Lysosomal Storage Disorders Research
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed

Funders: National Health and Medical Research Council, Actelion Pharmaceuticals
Award: Optimising speech assessment and treatment in frontotemporal dementia
OpenAlex ID: W3036712340
FWCI: 0.804
Cites: 33
Cited by: 10
Related to: 10
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