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Benserazide racemate and enantiomers induce fetal globin gene expression in vivo: Studies to guide clinical development for beta thalassemia and sickle cell disease

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Year: 2021
Type: article
Source: Blood Cells Molecules and Diseases
DOI: 10.1016/j.bcmd.2021.102561
Authors: Betty S. Pace, Susan Perrine, Biaoru Li, Levi Makala, Hongyan Xu, Mayuko Takezaki, Roman F. Wolf, Amy Wang, Xin Xu, Junfeng Huang, Asaf Alimardanov, Gregory J. Tawa, Jose Sangerman, Aidan Faller, Wei Zheng, London Toney, Sharie J. Haugabook
Institutions: Augusta University, Boston University, Phoenicia Biosciences (United States), University of Oklahoma Health Sciences Center, National Institutes of Health, National Center for Advancing Translational Sciences
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: bronze

Funders: School of Medicine, Boston University, National Institutes of Health, National Heart, Lung, and Blood Institute, National Cancer Institute, National Institute of Diabetes and Digestive and Kidney Diseases, National Center for Advancing Translational Sciences
Awards: G386607036, G5888954722, Development of a clinical hemoglobin modulator, Novel Globin Gene Modulators, Repurposing an EU Therapeutic for Hemoglobinopathies
OpenAlex ID: W3138399121
FWCI: 2.28
Cites: 57
Cited by: 17
Related to: 10
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