Work

Universal Gene Correction Approaches for β-hemoglobinopathies Using CRISPR-Cas9 and Adeno-Associated Virus Serotype 6 Donor Templates

Year: 2021

Type: article

Source: The CRISPR Journal

DOI: 10.1089/crispr.2020.0141

Authors: Andrés Lamsfus-Calle, Alberto Daniel-Moreno, Guillermo Ureña-Bailén, Jennifer Rottenberger, Janani Raju, Thomas Epting, Sabina Marciano, Lukas Heumos, Praveen Baskaran, Justin S Antony, Rupert Handgretinger, Markus Mezger

Institutions: University Children's Hospital Tübingen, University of Tübingen, University of Freiburg, University Medical Center Freiburg, Quantitative Biology Center

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W3155043640

FWCI: 0.965

Cites: 38

Cited by: 9

Related to: 10