Work

Relationship of pharmacokinetics and pharmacodynamics to apitegromab efficacy in patients with later-onset spinal muscular atrophy (Types 2 and 3 SMA): Results from the TOPAZ study

Year: 2021

Type: article

Source: Journal of the Neurological Sciences

DOI: 10.1016/j.jns.2021.118388

Authors: Thomas Crawford, Amy Place, Doreen Barrett, Shaun Cote, George Nomikos, Guochen Song, Sanela Bilic, Ashish Kalra, Mara Sadanowicz, Janet O'Neil, Ryan Iarrobino, Nathalie Kertesz, Yung Chyung

Institutions: Johns Hopkins University, Johns Hopkins Medicine, Scholar Rock (United States)

Language: English

Topic: Neurogenetic and Muscular Disorders Research

Subfield: Genetics (clinical)

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W3205944481

FWCI:

Cites:

Cited by:

Related to: 10