Pre-Clinical Development of a Highly Efficient TALEN ®-Based Correction of the β-Globin Gene in Patient-Derived Hematopoietic Stem and Progenitor Cells (HSPCs) to Treat Sickle Cell Disease
Year: 2021
Type: conference-abstract
Source: Blood
Authors: Arianna Moiani, Patrick Hong, Gil Letort, Sabrina Lizot, Alexa Chirinos, Sonal Temburni-Blake, Sara Nik, Louisa Mayer, Sophie Leduc, Noemie Pinard, Chloe Foray, Alex Boyne, Selena Kazancioglu, Giacomo Frati, Tristan Felix, Anne Chalumeau, Annarita Miccio, Mathilde Dusseaux, Agnès Gouble, Mark G. Frattini, Carrie Brownstein, Aymeric Duclert, Cecile Shiffer-Mannoui, Alexandre Juillerat, Philippe Duchateau, Julien Valton
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W3213729902