Preliminary Safety and Efficacy Results of EDI001: An Investigator Initiated Trial on CRISPR/Cas9-Modified Autologous CD34+ Hematopoietic Stem and Progenitor Cells for Patients with Transfusion Dependent β-Thalassemia
Year: 2022
Type: article
Source: Blood
Authors: Jun Shi, Riguo Fang, Zhen Gao, Zhongyu Shi, Zhexiang Kuang, Yongjian Zhang, Lele Zhang, Huihui Yang, Yingchi Zhang, Dehui Zou, Liwei Fang, Jiali Sun, Qiang Li, Yao Zou, Hong Pan, Jingyu Zhao, Liyun Li, Xiao Yu, Jing Xu, Chun Xu, Yanjie Liu, Weiwei Wang, Jia Shi, Jie Liu, Jia Wang, Nian Shi, Lei Yang, Weiqiang Wang, Suyi Li, Moye Shi, Xiaoshuang Zhang, Pengfei Yuan, Wensheng Wei, Dong Wei, Tao Cheng
Language: English
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4310107589
