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Favorable outcome of hematopoietic stem cell transplantation in late-onset Krabbe disease

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Year: 2023
Type: article
Study design: Case Report
Source: Brain and Development
DOI: 10.1016/j.braindev.2023.04.001
Authors: Akihiko Mitsutake, Takashi Matsukawa, Atsushi Iwata, Hiroyuki Ishiura, Jun Mitsui, Harushi Mori, Takashi Toya, Akira Honda, Mineo Kurokawa, Norio Sakai, Shoji Tsuji, Tatsushi Toda
Institutions: University of Tokyo Hospital, Mita Hospital, Tokyo Metropolitan Geriatric Hospital, Okayama University, The University of Tokyo, Jichi Medical University, Tokyo Metropolitan Komagome Hospital, The University of Osaka, International University of Health and Welfare
Language: English

Topic: Lysosomal Storage Disorders Research
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: bronze

Funder: Japan Society for the Promotion of Science
Award: Research on neurodegenerative disorders
OpenAlex ID: W4366277583
FWCI: 1.854
Cites: 10
Cited by: 8
Related to: 10
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