Work

Long-Term Follow-Up of Onasemnogene Abeparvovec Gene Therapy in Patients with Spinal Muscular Atrophy Type 1 (P7-9.006)

Year: 2023

Type: article

Source: Neurology

DOI: 10.1212/wnl.0000000000202549

Authors: Jerry Mendell, Melissa Wigderson, Iulian Alecu, Lina Yang, Lesa Mehl, Anne Connolly

Institutions: Nationwide Children's Hospital, Novartis Gene Therapies, Inc. (United States), Novartis (Switzerland), Novartis Institutes for BioMedical Research

Language: English

Topic: Neurogenetic and Muscular Disorders Research

Subfield: Genetics (clinical)

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4367303247

FWCI: 1.623

Cites:

Cited by: 7

Related to: 10