Work

Gene therapy prevents disease and death from non-ketotic hyperglycinemia

Year: 2025

Type: preprint

Source: bioRxiv (Cold Spring Harbor Laboratory)

DOI: 10.1101/2025.03.26.645560

Authors: Alejandro Lopez-Ramirez, Adviti Bali, Md Suhail Alam, Prasad Padmanabhan, Shaun Calhoun, Caroline Bickerton, Ana L. Flores-Mireles, Kasturi Haldar

Institution: University of Notre Dame

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4409010237

Cites: 46

Cited by: 3

Related to: 10