Preclinical Pharmacology and Toxicology of intrathecally infused AAV9-hABCD1, a gene therapy candidate for AMN, in Non-Human Primates (S29.002)
Year: 2022
Type: article
Source: Neurology
Authors: Vidyullatha Vasireddy, Sean Clark, Mark Cartwright, Karen Kozarsky, David Anderson
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W4389374000
